Outcome measures and clinical assessment instruments in neuromuscular disease

Jeffrey Rosenfeld, Carlayne E Jackson

Research output: Chapter in Book/Report/Conference proceedingChapter

Abstract

This chapter reviews issues which result from consideration of the optimal outcome measures. By its nature, the process of measurement requires reducing a dynamic process (the patient dealing with their disability) to a 2-dimensional snapshot (the patient's score at one point in time) that will be used to reflect a patient's condition. Measurement is usually an imperfect process, especially when relatively small treatment effects are expected. Multiple examples of available treatment instruments will be reviewed with an emphasis on their benefits and limitations for future use.

Original languageEnglish (US)
Title of host publicationNeuromuscular Disorders in Clinical Practice
PublisherSpringer New York
Pages287-326
Number of pages40
Volume9781461465676
ISBN (Print)9781461465676, 1461465664, 9781461465669
DOIs
StatePublished - Nov 1 2014
Externally publishedYes

Keywords

  • clinical trials
  • outcome measures
  • quality of life
  • sensitivity
  • specificity

ASJC Scopus subject areas

  • Medicine(all)

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