Outcome measures and clinical assessment instruments in neuromuscular disease

Jeffrey Rosenfeld; Carlayne E Jackson

doi:10.1007/978-1-4614-6567-6_15

Outcome measures and clinical assessment instruments in neuromuscular disease

Research output: Chapter in Book/Report/Conference proceeding › Chapter

Abstract

This chapter reviews issues which result from consideration of the optimal outcome measures. By its nature, the process of measurement requires reducing a dynamic process (the patient dealing with their disability) to a 2-dimensional snapshot (the patient's score at one point in time) that will be used to reflect a patient's condition. Measurement is usually an imperfect process, especially when relatively small treatment effects are expected. Multiple examples of available treatment instruments will be reviewed with an emphasis on their benefits and limitations for future use.

Original language	English (US)
Title of host publication	Neuromuscular Disorders in Clinical Practice
Publisher	Springer New York
Pages	287-326
Number of pages	40
Volume	9781461465676
ISBN (Print)	9781461465676, 1461465664, 9781461465669
DOIs	https://doi.org/10.1007/978-1-4614-6567-6_15
Publication status	Published - Nov 1 2014
Externally published	Yes

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Keywords

clinical trials
outcome measures
quality of life
sensitivity
specificity

ASJC Scopus subject areas

Medicine(all)

Cite this

Rosenfeld, J., & Jackson, C. E. (2014). Outcome measures and clinical assessment instruments in neuromuscular disease. In Neuromuscular Disorders in Clinical Practice (Vol. 9781461465676, pp. 287-326). Springer New York. https://doi.org/10.1007/978-1-4614-6567-6_15

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Access to Document

10.1007/978-1-4614-6567-6_15